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Structural Features of Small Molecules Targeting the RNA Repeat Expansion That Causes Genetically Defined ALS/FTD.
Ursu, Andrei; Wang, Kye Won; Bush, Jessica A; Choudhary, Shruti; Chen, Jonathan L; Baisden, Jared T; Zhang, Yong-Jie; Gendron, Tania F; Petrucelli, Leonard; Yildirim, Ilyas; Disney, Matthew D.
Afiliación
  • Ursu A; Department of Chemistry, The Scripps Research Institute, 130 Scripps Way, Jupiter, Florida 33458, United States.
  • Wang KW; Department of Chemistry and Biochemistry, Florida Atlantic University, Jupiter, Florida 33458, United States.
  • Bush JA; Department of Chemistry, The Scripps Research Institute, 130 Scripps Way, Jupiter, Florida 33458, United States.
  • Choudhary S; Department of Chemistry, The Scripps Research Institute, 130 Scripps Way, Jupiter, Florida 33458, United States.
  • Chen JL; Department of Chemistry, The Scripps Research Institute, 130 Scripps Way, Jupiter, Florida 33458, United States.
  • Baisden JT; Department of Chemistry, The Scripps Research Institute, 130 Scripps Way, Jupiter, Florida 33458, United States.
  • Zhang YJ; Department of Neuroscience, Mayo Clinic, 4500 San Pablo Rd., Jacksonville, Florida 32224, United States.
  • Gendron TF; Department of Neuroscience, Mayo Clinic, 4500 San Pablo Rd., Jacksonville, Florida 32224, United States.
  • Petrucelli L; Department of Neuroscience, Mayo Clinic, 4500 San Pablo Rd., Jacksonville, Florida 32224, United States.
  • Yildirim I; Department of Chemistry and Biochemistry, Florida Atlantic University, Jupiter, Florida 33458, United States.
  • Disney MD; Department of Chemistry, The Scripps Research Institute, 130 Scripps Way, Jupiter, Florida 33458, United States.
ACS Chem Biol ; 15(12): 3112-3123, 2020 12 18.
Article en En | MEDLINE | ID: mdl-33196168

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: ARN / Bibliotecas de Moléculas Pequeñas / Demencia Frontotemporal / Esclerosis Amiotrófica Lateral Tipo de estudio: Etiology_studies / Prognostic_studies Límite: Humans Idioma: En Revista: ACS Chem Biol Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: ARN / Bibliotecas de Moléculas Pequeñas / Demencia Frontotemporal / Esclerosis Amiotrófica Lateral Tipo de estudio: Etiology_studies / Prognostic_studies Límite: Humans Idioma: En Revista: ACS Chem Biol Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos