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Lovo-cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB-206 study.
Kanter, Julie; Thompson, Alexis A; Pierciey, Francis J; Hsieh, Matthew; Uchida, Naoya; Leboulch, Philippe; Schmidt, Manfred; Bonner, Melissa; Guo, Ruiting; Miller, Alex; Ribeil, Jean-Antoine; Davidson, David; Asmal, Mohammed; Walters, Mark C; Tisdale, John F.
Afiliación
  • Kanter J; Department of Hematology-Oncology, University of Alabama Birmingham, Birmingham, Alabama, USA.
  • Thompson AA; Division of Hematology, Oncology, and Stem Cell Transplantation, Northwestern University Feinberg School of Medicine, Chicago, Illinois, USA.
  • Pierciey FJ; Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA.
  • Hsieh M; bluebird bio, Inc., Somerville, Massachusetts, USA.
  • Uchida N; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute/National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, Maryland, USA.
  • Leboulch P; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute/National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, Maryland, USA.
  • Schmidt M; Commissariat à l'énergie atomique et aux énergies alternatives, Institute of Emerging Disease and Innovative Therapies, Fontenay-aux-Roses, France.
  • Bonner M; Department of Medicine, Brigham & Women's Hospital and Harvard Medical School, Boston, Massachusetts, USA.
  • Guo R; GeneWerk GmbH, Heidelberg, Germany.
  • Miller A; bluebird bio, Inc., Somerville, Massachusetts, USA.
  • Ribeil JA; bluebird bio, Inc., Somerville, Massachusetts, USA.
  • Davidson D; bluebird bio, Inc., Somerville, Massachusetts, USA.
  • Asmal M; bluebird bio, Inc., Somerville, Massachusetts, USA.
  • Walters MC; bluebird bio, Inc., Somerville, Massachusetts, USA.
  • Tisdale JF; bluebird bio, Inc., Somerville, Massachusetts, USA.
Am J Hematol ; 98(1): 11-22, 2023 01.
Article en En | MEDLINE | ID: mdl-36161320

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Trasplante de Células Madre Hematopoyéticas / Anemia de Células Falciformes Límite: Humans Idioma: En Revista: Am J Hematol Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Trasplante de Células Madre Hematopoyéticas / Anemia de Células Falciformes Límite: Humans Idioma: En Revista: Am J Hematol Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos