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Dramatic elevation in urinary amino terminal titin fragment excretion quantified by immunoassay in Duchenne muscular dystrophy patients and in dystrophin deficient rodents.
Robertson, Alan S; Majchrzak, Mark J; Smith, Courtney M; Gagnon, Robert C; Devidze, Nino; Banks, Glen B; Little, Sean C; Nabbie, Fizal; Bounous, Denise I; DiPiero, Janet; Jacobsen, Leslie K; Bristow, Linda J; Ahlijanian, Michael K; Stimpson, Stephen A.
Afiliação
  • Robertson AS; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Majchrzak MJ; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Smith CM; Department of Pharmacology, Yale University, New Haven, CT, USA.
  • Gagnon RC; Non-Clinical Biostatistics, Bristol-Myers Squibb, Lawrenceville, NJ, USA.
  • Devidze N; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Banks GB; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Little SC; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Nabbie F; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Bounous DI; Discovery Toxicology Clinical Pathology Laboratory, Bristol-Myers Squibb, Lawrenceville, NJ, USA.
  • DiPiero J; Discovery Toxicology Clinical Pathology Laboratory, Bristol-Myers Squibb, Lawrenceville, NJ, USA.
  • Jacobsen LK; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Bristow LJ; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
  • Ahlijanian MK; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA. Electronic address: michael.ahlijanian@bms.com.
  • Stimpson SA; Genetically Defined Diseases, Bristol-Myers Squibb, Wallingford, CT, USA.
Neuromuscul Disord ; 27(7): 635-645, 2017 Jul.
Article em En | MEDLINE | ID: mdl-28554556

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Distrofia Muscular de Duchenne / Conectina Tipo de estudo: Observational_studies / Prevalence_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Animals / Child / Child, preschool / Humans Idioma: En Revista: Neuromuscul Disord Assunto da revista: NEUROLOGIA Ano de publicação: 2017 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Distrofia Muscular de Duchenne / Conectina Tipo de estudo: Observational_studies / Prevalence_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Animals / Child / Child, preschool / Humans Idioma: En Revista: Neuromuscul Disord Assunto da revista: NEUROLOGIA Ano de publicação: 2017 Tipo de documento: Article País de afiliação: Estados Unidos