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Optimized Adeno-Associated Viral-Mediated Human Factor VIII Gene Therapy in Cynomolgus Macaques.
Greig, Jenny A; Nordin, Jayme M L; White, John W; Wang, Qiang; Bote, Erin; Goode, Tamara; Calcedo, Roberto; Wadsworth, Samuel; Wang, Lili; Wilson, James M.
Afiliação
  • Greig JA; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Nordin JML; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • White JW; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Wang Q; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Bote E; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Goode T; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Calcedo R; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Wadsworth S; 2 Ultragenyx Gene Therapy, Cambridge, Massachusetts.
  • Wang L; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Wilson JM; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
Hum Gene Ther ; 2018 Jul 23.
Article em En | MEDLINE | ID: mdl-29890905

Texto completo: 1 Bases de dados: MEDLINE Tipo de estudo: Prognostic_studies / Risk_factors_studies Idioma: En Revista: Hum Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Bases de dados: MEDLINE Tipo de estudo: Prognostic_studies / Risk_factors_studies Idioma: En Revista: Hum Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2018 Tipo de documento: Article