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Validation of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO© ).
Taher, Ali; Cappellini, Maria Domenica; Viprakasit, Vip; Sutcharitchan, Pranee; Mahmoud, Dalia; Laadem, Abderrahmane; Khan, Anzalee; Gwaltney, Chad; Harding, Gale; Attie, Kenneth; Zhang, Xiaosha; Zou, Jun; Pariseau, Joseph; Henry Hu, X; Kattamis, Antonis.
Afiliação
  • Taher A; American University of Beirut Medical Center, Beirut, Lebanon.
  • Cappellini MD; Ospedale Maggiore Policlinico IRCCS, University of Milan, Milan, Italy.
  • Viprakasit V; Siriraj Hospital, Mahidol University, Bangkok, Thailand.
  • Sutcharitchan P; Chulalongkorn University, Bangkok, Thailand.
  • Mahmoud D; Celgene Corporation, Summit, New Jersey.
  • Laadem A; Celgene Corporation, Summit, New Jersey.
  • Khan A; Nathan S. Kline Institute for Psychiatric Research, Orangeburg, New York.
  • Gwaltney C; NeuroCog Trials, Durham, North Carolina.
  • Harding G; ERT, Philadelphia, Pennsylvania.
  • Attie K; Evidera, Bethesda, Maryland.
  • Zhang X; Acceleron Pharma, Cambridge, Massachusetts.
  • Zou J; Acceleron Pharma, Cambridge, Massachusetts.
  • Pariseau J; Celgene Corporation, Summit, New Jersey.
  • Henry Hu X; Celgene Corporation, Summit, New Jersey.
  • Kattamis A; Celgene Corporation, Summit, New Jersey.
Am J Hematol ; 94(2): 177-183, 2019 02.
Article em En | MEDLINE | ID: mdl-30394570

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Talassemia beta / Medidas de Resultados Relatados pelo Paciente Tipo de estudo: Clinical_trials / Diagnostic_studies / Observational_studies Limite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Am J Hematol Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Líbano

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Talassemia beta / Medidas de Resultados Relatados pelo Paciente Tipo de estudo: Clinical_trials / Diagnostic_studies / Observational_studies Limite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Revista: Am J Hematol Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Líbano