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Lower Exposure to Busulfan Allows for Stable Engraftment of Donor Hematopoietic Stem Cells in Children with Mucopolysaccharidosis Type I: A Case Report of Four Patients.
Shukla, Praveen; Dvorak, Christopher C; Long-Boyle, Janel; Kharbanda, Sandhya.
Afiliação
  • Shukla P; Department of Clinical Pharmacy, University of California San Francisco, 600 16th Street, Room N474F, San Francisco, CA 94158-0622, USA.
  • Dvorak CC; Division of Pediatric Allergy, Immunology, and Blood and Marrow Transplant, University of California San Francisco, Benioff Children's Hospital, 550 16th Street, Floor 4, San Francisco, CA 94143-0434, USA.
  • Long-Boyle J; Department of Clinical Pharmacy, University of California San Francisco, 600 16th Street, Room N474F, San Francisco, CA 94158-0622, USA.
  • Kharbanda S; Division of Pediatric Allergy, Immunology, and Blood and Marrow Transplant, University of California San Francisco, Benioff Children's Hospital, 550 16th Street, Floor 4, San Francisco, CA 94143-0434, USA.
Int J Mol Sci ; 21(16)2020 Aug 06.
Article em En | MEDLINE | ID: mdl-32781600

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Bussulfano / Mucopolissacaridose I / Transplante de Células-Tronco Hematopoéticas Tipo de estudo: Guideline / Prognostic_studies Limite: Child / Female / Humans / Infant / Male Idioma: En Revista: Int J Mol Sci Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Bussulfano / Mucopolissacaridose I / Transplante de Células-Tronco Hematopoéticas Tipo de estudo: Guideline / Prognostic_studies Limite: Child / Female / Humans / Infant / Male Idioma: En Revista: Int J Mol Sci Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Estados Unidos