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Central nervous system pathology in preclinical MPS IIIB dogs reveals progressive changes in clinically relevant brain regions.
Egeland, Martin T; Tarczyluk-Wells, Marta M; Asmar, Melissa M; Adintori, Evan G; Lawrence, Roger; Snella, Elizabeth M; Jens, Jackie K; Crawford, Brett E; Wait, Jill C M; McCullagh, Emma; Pinkstaff, Jason; Cooper, Jonathan D; Ellinwood, N Matthew.
Afiliação
  • Egeland MT; The Lundquist Institute at Harbor-UCLA Medical Center, and David Geffen School of Medicine, UCLA, Torrance, CA, USA.
  • Tarczyluk-Wells MM; King's College London, Institute of Psychiatry, Psychology and Neuroscience, Maurice Wohl Clinical Neuroscience Institute, London, UK.
  • Asmar MM; King's College London, Institute of Psychiatry, Psychology and Neuroscience, Maurice Wohl Clinical Neuroscience Institute, London, UK.
  • Adintori EG; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Lawrence R; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Snella EM; Iowa State University, Ames, IA, USA.
  • Jens JK; Iowa State University, Ames, IA, USA.
  • Crawford BE; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Wait JCM; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • McCullagh E; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Pinkstaff J; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Cooper JD; The Lundquist Institute at Harbor-UCLA Medical Center, and David Geffen School of Medicine, UCLA, Torrance, CA, USA. cooperjd@wustl.edu.
  • Ellinwood NM; King's College London, Institute of Psychiatry, Psychology and Neuroscience, Maurice Wohl Clinical Neuroscience Institute, London, UK. cooperjd@wustl.edu.
Sci Rep ; 10(1): 20365, 2020 11 23.
Article em En | MEDLINE | ID: mdl-33230178

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Acetilglucosaminidase / Cerebelo / Córtex Cerebral / Prosencéfalo / Mucopolissacaridose III / Doenças do Cão Tipo de estudo: Prognostic_studies Limite: Animals / Female / Humans / Male Idioma: En Revista: Sci Rep Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Acetilglucosaminidase / Cerebelo / Córtex Cerebral / Prosencéfalo / Mucopolissacaridose III / Doenças do Cão Tipo de estudo: Prognostic_studies Limite: Animals / Female / Humans / Male Idioma: En Revista: Sci Rep Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Estados Unidos