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Long term clinical effectiveness of ivacaftor in people with the G551D CFTR mutation.
Guimbellot, J S; Baines, A; Paynter, A; Heltshe, S L; VanDalfsen, J; Jain, M; Rowe, S M; Sagel, S D.
Afiliação
  • Guimbellot JS; Gregory Fleming James Cystic Fibrosis Research Center, University of Alabama at Birmingham (UAB), Birmingham, AL, United States; Department of Pediatrics, Division of Pulmonary and Sleep Medicine, UAB, Birmingham, AL, United States. Electronic address: jguimbellot@peds.uab.edu.
  • Baines A; CFF Therapeutics Development Network Coordinating Center, Seattle Children's Research Institute, Seattle, WA, United States.
  • Paynter A; CFF Therapeutics Development Network Coordinating Center, Seattle Children's Research Institute, Seattle, WA, United States.
  • Heltshe SL; CFF Therapeutics Development Network Coordinating Center, Seattle Children's Research Institute, Seattle, WA, United States; Department of Pediatrics, Division of Pulmonary and Sleep Medicine, University of Washington, Seattle WA, United States.
  • VanDalfsen J; CFF Therapeutics Development Network Coordinating Center, Seattle Children's Research Institute, Seattle, WA, United States.
  • Jain M; Department of Medicine, Division of Pulmonary and Critical Care Medicine, Northwestern University Feinberg School of Medicine, Chicago, IL, United States.
  • Rowe SM; Gregory Fleming James Cystic Fibrosis Research Center, University of Alabama at Birmingham (UAB), Birmingham, AL, United States; Department of Pediatrics, Division of Pulmonary and Sleep Medicine, UAB, Birmingham, AL, United States; Department of Medicine, Division of Pulmonary, Allergy, and Critica
  • Sagel SD; Department of Pediatrics, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, CO, United States.
J Cyst Fibros ; 20(2): 213-219, 2021 03.
Article em En | MEDLINE | ID: mdl-33249004

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Agonistas dos Canais de Cloreto / Aminofenóis Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Female / Humans / Male País/Região como assunto: America do norte Idioma: En Revista: J Cyst Fibros Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Agonistas dos Canais de Cloreto / Aminofenóis Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Female / Humans / Male País/Região como assunto: America do norte Idioma: En Revista: J Cyst Fibros Ano de publicação: 2021 Tipo de documento: Article