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Gene therapy restores mitochondrial function and protects retinal ganglion cells in optic neuropathy induced by a mito-targeted mutant ND1 gene.
Liu, Yuan; Eastwood, Jeremy D; Alba, Diego E; Velmurugan, Sindhu; Sun, Ning; Porciatti, Vittorio; Lee, Richard K; Hauswirth, William W; Guy, John; Yu, Hong.
Afiliação
  • Liu Y; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA.
  • Eastwood JD; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA.
  • Alba DE; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA.
  • Velmurugan S; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA.
  • Sun N; Department of Biostatistics, Robert Stempel College of Public Health & Social Work, Florida International University, Miami, FL, USA.
  • Porciatti V; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA.
  • Lee RK; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA. rlee@med.miami.edu.
  • Hauswirth WW; Department of Ophthalmology, College of Medicine, University of Florida, Gainesville, FL, USA.
  • Guy J; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA.
  • Yu H; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, USA. hyu3@med.miami.edu.
Gene Ther ; 29(6): 368-378, 2022 06.
Article em En | MEDLINE | ID: mdl-35383288

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Células Ganglionares da Retina / Atrofia Óptica Hereditária de Leber Limite: Animals / Humans Idioma: En Revista: Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Células Ganglionares da Retina / Atrofia Óptica Hereditária de Leber Limite: Animals / Humans Idioma: En Revista: Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos