Your browser doesn't support javascript.
loading
Treatment of Fabry Disease management with migalastat-outcome from a prospective 24 months observational multicenter study (FAMOUS).
Lenders, Malte; Nordbeck, Peter; Kurschat, Christine; Eveslage, Maria; Karabul, Nesrin; Kaufeld, Jessica; Hennermann, Julia B; Patten, Monica; Cybulla, Markus; Müntze, Jonas; Üçeyler, Nurcan; Liu, Dan; Das, Anibh M; Sommer, Claudia; Pogoda, Christian; Reiermann, Stefanie; Duning, Thomas; Gaedeke, Jens; von Cossel, Katharina; Blaschke, Daniela; Brand, Stefan-Martin; Mann, W Alexander; Kampmann, Christoph; Muschol, Nicole; Canaan-Kühl, Sima; Brand, Eva.
Afiliação
  • Lenders M; Department of Internal Medicine D, Interdisciplinary Fabry Center (IFAZ), University Hospital Münster, Münster, Germany.
  • Nordbeck P; Department of Internal Medicine I, Comprehensive Heart Failure Center, Fabry Center for Interdisciplinary Therapy (FAZIT), University of Würzburg, Würzburg, Germany.
  • Kurschat C; Department II of Internal Medicine, Center for Molecular Medicine Cologne and Center for Rare Diseases, University of Cologne, Cologne, Germany.
  • Eveslage M; Institute of Biostatistics and Clinical Research (IBKF), University of Münster, Münster, Germany.
  • Karabul N; Endokrinologikum Frankfurt, Center of Hormonal and Metabolic Diseases, Rheumatology, Osteology and Neurology, Frankfurt, Germany.
  • Kaufeld J; Department of Nephrology and Hypertension, Hannover Medical School, Hannover, Germany.
  • Hennermann JB; Department for Pediatric and Adolescent Medicine, University Medical Center Mainz, Villa Metabolica, Mainz, Germany.
  • Patten M; Department of General and Interventional Cardiology, University Heart Center Hamburg, Hamburg, Germany.
  • Cybulla M; Department of Nephrology and Rheumatology, FGM, Center of Internal Medicine, Müllheim, Germany.
  • Müntze J; Department of Internal Medicine I, Comprehensive Heart Failure Center, Fabry Center for Interdisciplinary Therapy (FAZIT), University of Würzburg, Würzburg, Germany.
  • Üçeyler N; Department of Neurology, University of Würzburg, Würzburg, Germany.
  • Liu D; Department of Internal Medicine I, Comprehensive Heart Failure Center, Fabry Center for Interdisciplinary Therapy (FAZIT), University of Würzburg, Würzburg, Germany.
  • Das AM; Department of Paediatrics, Hannover Medical School, Hannover, Germany.
  • Sommer C; Department of Neurology, University of Würzburg, Würzburg, Germany.
  • Pogoda C; Department of Cardiology I-Coronary and Peripheral Vascular Disease, Heart Failure, Interdisciplinary Fabry Center (IFAZ), University Hospital Münster, Münster, Germany.
  • Reiermann S; Department of Internal Medicine D, Interdisciplinary Fabry Center (IFAZ), University Hospital Münster, Münster, Germany.
  • Duning T; Department of Neurology, Interdisciplinary Fabry Center (IFAZ), University Hospital Münster, Münster, Germany.
  • Gaedeke J; Medizinische Klinik mit Schwerpunkt Nephrologie und Internistische Intensivmedizin, Fabry Zentrum, Zentrum für seltene Nierenerkrankungen (CeRKiD), Campus Charité Mitte, Charité-Universitätsmedizin Berlin, Berlin, Germany.
  • von Cossel K; Department of Pediatrics, University Medical Center Hamburg, Eppendorf, Hamburg, Germany.
  • Blaschke D; Department of Medicine, Division of Cardiology, Charité, Campus Virchow-Klinikum, Berlin, Germany.
  • Brand SM; Institute of Sports Medicine, Molecular Genetics of Cardiovascular Disease, Interdisciplinary Fabry Center (IFAZ), University Hospital Münster, Münster, Germany.
  • Mann WA; Endokrinologikum Frankfurt, Center of Hormonal and Metabolic Diseases, Rheumatology, Osteology and Neurology, Frankfurt, Germany.
  • Kampmann C; Department for Pediatric and Adolescent Medicine, University Medical Center Mainz, Villa Metabolica, Mainz, Germany.
  • Muschol N; Department of Pediatrics, University Medical Center Hamburg, Eppendorf, Hamburg, Germany.
  • Canaan-Kühl S; Medizinische Klinik mit Schwerpunkt Nephrologie und Internistische Intensivmedizin, Fabry Zentrum, Zentrum für seltene Nierenerkrankungen (CeRKiD), Campus Charité Mitte, Charité-Universitätsmedizin Berlin, Berlin, Germany.
  • Brand E; Department of Internal Medicine D, Interdisciplinary Fabry Center (IFAZ), University Hospital Münster, Münster, Germany.
Eur Heart J Cardiovasc Pharmacother ; 8(3): 272-281, 2022 05 05.
Article em En | MEDLINE | ID: mdl-35512362

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Doença de Fabry Tipo de estudo: Clinical_trials / Diagnostic_studies / Observational_studies Limite: Female / Humans / Male Idioma: En Revista: Eur Heart J Cardiovasc Pharmacother Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Doença de Fabry Tipo de estudo: Clinical_trials / Diagnostic_studies / Observational_studies Limite: Female / Humans / Male Idioma: En Revista: Eur Heart J Cardiovasc Pharmacother Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Alemanha