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Maralixibat Treatment Response in Alagille Syndrome is Associated with Improved Health-Related Quality of Life.
Kamath, Binita M; Goldstein, Andrea; Howard, Robin; Garner, Will; Vig, Pamela; Marden, Jessica R; Billmyer, Emma; Anderson, Annika; Kirson, Noam; Jacquemin, Emmanuel; Gonzales, Emmanuel.
Afiliação
  • Kamath BM; Division of Gastroenterology, Hepatology and Nutrition, The Hospital for Sick Children and University of Toronto, Toronto, Canada. Electronic address: binita.kamath@sickkids.ca.
  • Goldstein A; Mirum Pharmaceuticals, Inc., Foster City, CA.
  • Howard R; Mirum Pharmaceuticals, Inc., Foster City, CA.
  • Garner W; Mirum Pharmaceuticals, Inc., Foster City, CA.
  • Vig P; Mirum Pharmaceuticals, Inc., Foster City, CA.
  • Marden JR; Analysis Group, Inc., Boston, MA.
  • Billmyer E; Analysis Group, Inc., Boston, MA.
  • Anderson A; Analysis Group, Inc., Boston, MA.
  • Kirson N; Analysis Group, Inc., Boston, MA.
  • Jacquemin E; Hépatologie et Transplantation Hépatique Pédiatriques, Centre de référence national de l'atrésie des voies biliaires et des cholestases génétiques, FSMR FILFOIE, Hôpital Bicêtre, AP-HP, Université Paris-Saclay, Kremlin-Bicêtre; INSERM UMR-1193, Hepatinov, Université Paris-Saclay, Orsay, France; Euro
  • Gonzales E; Hépatologie et Transplantation Hépatique Pédiatriques, Centre de référence national de l'atrésie des voies biliaires et des cholestases génétiques, FSMR FILFOIE, Hôpital Bicêtre, AP-HP, Université Paris-Saclay, Kremlin-Bicêtre; INSERM UMR-1193, Hepatinov, Université Paris-Saclay, Orsay, France; Euro
J Pediatr ; 252: 68-75.e5, 2023 01.
Article em En | MEDLINE | ID: mdl-36096175

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Qualidade de Vida / Síndrome de Alagille Tipo de estudo: Clinical_trials / Risk_factors_studies Limite: Child / Humans Idioma: En Revista: J Pediatr Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Qualidade de Vida / Síndrome de Alagille Tipo de estudo: Clinical_trials / Risk_factors_studies Limite: Child / Humans Idioma: En Revista: J Pediatr Ano de publicação: 2023 Tipo de documento: Article