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Liver-directed gene therapy for ornithine aminotransferase deficiency.
Boffa, Iolanda; Polishchuk, Elena; De Stefano, Lucia; Dell'Aquila, Fabio; Nusco, Edoardo; Marrocco, Elena; Audano, Matteo; Pedretti, Silvia; Caterino, Marianna; Bellezza, Ilaria; Ruoppolo, Margherita; Mitro, Nico; Cellini, Barbara; Auricchio, Alberto; Brunetti-Pierri, Nicola.
Afiliação
  • Boffa I; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • Polishchuk E; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • De Stefano L; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • Dell'Aquila F; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • Nusco E; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • Marrocco E; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • Audano M; Department of Pharmacology and Biomolecular Sciences, University of Milan, Milan, Italy.
  • Pedretti S; Department of Pharmacology and Biomolecular Sciences, University of Milan, Milan, Italy.
  • Caterino M; Department of Molecular Medicine and Medical Biotechnology, University of Naples "Federico II", Naples, Italy.
  • Bellezza I; CEINGE - Biotecnologie Avanzate s.c.a.r.l., Naples, Italy.
  • Ruoppolo M; Department of Experimental Medicine, Section of Physiology and Biochemistry, University of Perugia, Perugia, Italy.
  • Mitro N; Department of Molecular Medicine and Medical Biotechnology, University of Naples "Federico II", Naples, Italy.
  • Cellini B; CEINGE - Biotecnologie Avanzate s.c.a.r.l., Naples, Italy.
  • Auricchio A; Department of Pharmacology and Biomolecular Sciences, University of Milan, Milan, Italy.
  • Brunetti-Pierri N; Department of Experimental Oncology, IEO, European Institute of Oncology IRCCS, Milan, Italy.
EMBO Mol Med ; 15(4): e17033, 2023 04 11.
Article em En | MEDLINE | ID: mdl-36647689

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Degeneração Retiniana / Atrofia Girata Limite: Animals Idioma: En Revista: EMBO Mol Med Assunto da revista: BIOLOGIA MOLECULAR Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Bases de dados: MEDLINE Assunto principal: Degeneração Retiniana / Atrofia Girata Limite: Animals Idioma: En Revista: EMBO Mol Med Assunto da revista: BIOLOGIA MOLECULAR Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Itália