Pharmacological Therapies of Spinal Muscular Atrophy: A Narrative Review of Preclinical, Clinical-Experimental, and Real-World Evidence.

Crisafulli, Salvatore; Boccanegra, Brigida; Vitturi, Giacomo; Trifirò, Gianluca; De Luca, Annamaria

Crisafulli, Salvatore; Boccanegra, Brigida; Vitturi, Giacomo; Trifirò, Gianluca; De Luca, Annamaria.

Afiliação

Crisafulli S; Department of Medicine, University of Verona, Piazzale Ludovico Antonio Scuro 10, 37124 Verona, Italy.
Boccanegra B; Department of Pharmacy-Drug Sciences, University of Bari "Aldo Moro", Via E. Orabona 4, 70125 Bari, Italy.
Vitturi G; Department of Diagnostics and Public Health, University of Verona, Piazzale Ludovico Antonio Scuro 10, 37124 Verona, Italy.
Trifirò G; Department of Diagnostics and Public Health, University of Verona, Piazzale Ludovico Antonio Scuro 10, 37124 Verona, Italy.
De Luca A; Department of Pharmacy-Drug Sciences, University of Bari "Aldo Moro", Via E. Orabona 4, 70125 Bari, Italy.

Brain Sci ; 13(10)2023 Oct 10.

Article em En | MEDLINE | ID: mdl-37891814

Palavras-chave

nusinersen; onasemnogene abeparvovec; post-marketing evidence; pre-marketing evidence; risdiplam; spinal muscular atrophy

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Texto completo: 1 Bases de dados: MEDLINE Idioma: En Revista: Brain Sci Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Itália