Detalhe da pesquisa
1.
Engineered tRNAs suppress nonsense mutations in cells and in vivo.
Nature
; 618(7966): 842-848, 2023 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-37258671
2.
Lipid nanoparticle delivers phenylalanine ammonia lyase mRNA to the liver leading to catabolism and clearance of phenylalanine in a phenylketonuria mouse model.
Mol Genet Metab Rep
; 32: 100882, 2022 Sep.
Artigo
em Inglês
| MEDLINE | ID: mdl-35600090