Detalhe da pesquisa
1.
IgG-cleavage protein allows therapeutic AAV gene delivery in passively immunized MPS IIIA mice.
Gene Ther
; 30(3-4): 377-385, 2023 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-36253453
2.
Targeting the Root Cause of Mucopolysaccharidosis IIIA with a New scAAV9 Gene Replacement Vector.
Mol Ther Methods Clin Dev
; 19: 474-485, 2020 Dec 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-33313335