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Targeting Nonsense Mutations in Diseases with Translational Read-Through-Inducing Drugs (TRIDs).
Nagel-Wolfrum, Kerstin; Möller, Fabian; Penner, Inessa; Baasov, Timor; Wolfrum, Uwe.
Afiliação
  • Nagel-Wolfrum K; Department of Cell and Matrix Biology, Institute of Zoology, Johannes Gutenberg-University of Mainz, Johannes-von-Mueller-Weg 6, 55099, Mainz, Germany. nagelwol@uni-mainz.de.
  • Möller F; Focus Program Translational Neurosciences (FTN), Johannes Gutenberg-University of Mainz, 55122, Mainz, Germany. nagelwol@uni-mainz.de.
  • Penner I; Department of Cell and Matrix Biology, Institute of Zoology, Johannes Gutenberg-University of Mainz, Johannes-von-Mueller-Weg 6, 55099, Mainz, Germany.
  • Baasov T; Department of Cell and Matrix Biology, Institute of Zoology, Johannes Gutenberg-University of Mainz, Johannes-von-Mueller-Weg 6, 55099, Mainz, Germany.
  • Wolfrum U; Edith and Joseph Fischer Enzyme Inhibitors Laboratory, Schulich Faculty of Chemistry, Technion-Israel Institute of Technology, Haifa, Israel.
BioDrugs ; 30(2): 49-74, 2016 Apr.
Article em En | MEDLINE | ID: mdl-26886021

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Preparações Farmacêuticas / Códon sem Sentido / Doenças Genéticas Inatas Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: En Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Preparações Farmacêuticas / Códon sem Sentido / Doenças Genéticas Inatas Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: En Ano de publicação: 2016 Tipo de documento: Article