Development of Intrathecal AAV9 Gene Therapy for Giant Axonal Neuropathy.

Bailey, Rachel M; Armao, Diane; Nagabhushan Kalburgi, Sahana; Gray, Steven J

Bailey, Rachel M; Armao, Diane; Nagabhushan Kalburgi, Sahana; Gray, Steven J.

Afiliação

Bailey RM; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
Armao D; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
Nagabhushan Kalburgi S; Department of Radiology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
Gray SJ; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.

Mol Ther Methods Clin Dev ; 9: 160-171, 2018 Jun 15.

Article em En | MEDLINE | ID: mdl-29766026

Palavras-chave

AAV9; adeno-associated virus; biodistribution; dorsal root ganglia; fibroblast; gene therapy; giant axonal neuropathy; gigaxonin; intrathecal; sciatic nerve

Texto completo

Imprimir

XML

PubMed Links

Buscar no Google

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo

Imprimir

XML

PubMed Links

Buscar no Google

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2018 Tipo de documento: Article