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Short-Term Administration of Mycophenolate Is Well-Tolerated in CLN3 Disease (Juvenile Neuronal Ceroid Lipofuscinosis).
Augustine, Erika F; Beck, Christopher A; Adams, Heather R; Defendorf, Sara; Vierhile, Amy; Timm, Derek; Weimer, Jill M; Mink, Jonathan W; Marshall, Frederick J.
Afiliação
  • Augustine EF; Department of Neurology, University of Rochester Medical Center, Rochester, NY, USA. erika_augustine@urmc.rochester.edu.
  • Beck CA; Department of Pediatrics, University of Rochester Medical Center, Rochester, NY, USA. erika_augustine@urmc.rochester.edu.
  • Adams HR; Center for Health + Technology, University of Rochester Medical Center, Rochester, NY, USA. erika_augustine@urmc.rochester.edu.
  • Defendorf S; Department of Biostatistics and Computational Biology, University of Rochester Medical Center, Rochester, NY, USA.
  • Vierhile A; Department of Neurology, University of Rochester Medical Center, Rochester, NY, USA.
  • Timm D; Department of Pediatrics, University of Rochester Medical Center, Rochester, NY, USA.
  • Weimer JM; Pharmaceutical Product Development (PPD), Charlotte, NC, USA.
  • Mink JW; Department of Neurology, University of Rochester Medical Center, Rochester, NY, USA.
  • Marshall FJ; Department of Pediatrics, University of Rochester Medical Center, Rochester, NY, USA.
JIMD Rep ; 43: 117-124, 2019.
Article em En | MEDLINE | ID: mdl-29923092

Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Clinical_trials Idioma: En Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Clinical_trials Idioma: En Ano de publicação: 2019 Tipo de documento: Article