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Induction, titration, and maintenance dosing regimen in a phase 2 study of pegvaliase for control of blood phenylalanine in adults with phenylketonuria.
Zori, Roberto; Thomas, Janet A; Shur, Natasha; Rizzo, William B; Decker, Celeste; Rosen, Orli; Li, Mingjin; Schweighardt, Becky; Larimore, Kevin; Longo, Nicola.
Afiliação
  • Zori R; Department of Pediatrics in the College of Medicine, University of Florida, Gainesville, FL, USA. Electronic address: zorirt@pegs.ufl.edu.
  • Thomas JA; Clinical Genetics and Metabolism, Department of Pediatrics, University of Colorado School of Medicine, Aurora, CO, USA.
  • Shur N; Pediatrics Genetics Group, Albany Medical Center, Albany, NY, USA.
  • Rizzo WB; Department of Pediatrics, University of Nebraska Medical Center, Omaha, NE, USA.
  • Decker C; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Rosen O; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Li M; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Schweighardt B; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Larimore K; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Longo N; Division of Medical Genetics, University of Utah, Salt Lake City, UT, USA.
Mol Genet Metab ; 125(3): 217-227, 2018 11.
Article em En | MEDLINE | ID: mdl-30146451

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fenilalanina Amônia-Liase / Fenilalanina / Fenilcetonúrias / Proteínas Recombinantes Tipo de estudo: Guideline Limite: Adolescent / Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fenilalanina Amônia-Liase / Fenilalanina / Fenilcetonúrias / Proteínas Recombinantes Tipo de estudo: Guideline Limite: Adolescent / Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2018 Tipo de documento: Article