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Quality of life assessment in adult spinal muscular atrophy patients treated with nusinersen.
Bonanno, Silvia; Zanin, Riccardo; Bello, Luca; Tramacere, Irene; Bozzoni, Virginia; Caumo, Luca; Ferraro, Manfredi; Bortolani, Sara; Sorarù, Gianni; Silvestrini, Mauro; Vacchiano, Veria; Turri, Mara; Tanel, Raffaella; Liguori, Rocco; Coccia, Michela; Mantegazza, Renato Emilio; Mongini, Tiziana; Pegoraro, Elena; Maggi, Lorenzo.
Afiliação
  • Bonanno S; Neuroimmunology and Neuromuscular Disease Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, via Celoria 11, 20133, Milan, Italy.
  • Zanin R; Developmental Neurology, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.
  • Bello L; Department of Neuroscience, Myology Institute, University of Padova, Padua, Italy.
  • Tramacere I; Department of Research and Clinical Development, Scientific Directorate, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.
  • Bozzoni V; Department of Neuroscience, Myology Institute, University of Padova, Padua, Italy.
  • Caumo L; Department of Neuroscience, Myology Institute, University of Padova, Padua, Italy.
  • Ferraro M; Department of Neurosciences Rita Levi Montalcini, Neuromuscular Center, University of Torino, Turin, Italy.
  • Bortolani S; Department of Neurosciences Rita Levi Montalcini, Neuromuscular Center, University of Torino, Turin, Italy.
  • Sorarù G; Department of Neuroscience, Myology Institute, University of Padova, Padua, Italy.
  • Silvestrini M; Department of Neurological Sciences, Ospedali Riuniti di Ancona, Ancona, Italy.
  • Vacchiano V; Neurological Clinic, Marche Polytechnic University, Ancona, Italy.
  • Turri M; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy.
  • Tanel R; Department of Biomedical and Neuromotor Sciences, University of Bologna, Bologna, Italy.
  • Liguori R; Department of Neurology/Stroke Unit, San Maurizio Hospital, Bolzano, Italy.
  • Coccia M; Neurology Disease Unit, Osp. S. Chiara APSS, Trento, Italy.
  • Mantegazza RE; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy.
  • Mongini T; Department of Biomedical and Neuromotor Sciences, University of Bologna, Bologna, Italy.
  • Pegoraro E; Department of Neurological Sciences, Ospedali Riuniti di Ancona, Ancona, Italy.
  • Maggi L; Neuroimmunology and Neuromuscular Disease Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, via Celoria 11, 20133, Milan, Italy.
J Neurol ; 269(6): 3264-3275, 2022 Jun.
Article em En | MEDLINE | ID: mdl-34978620

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / Fragilidade Tipo de estudo: Observational_studies / Risk_factors_studies Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / Fragilidade Tipo de estudo: Observational_studies / Risk_factors_studies Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2022 Tipo de documento: Article