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Response of plasma microRNAs to nusinersen treatment in patients with SMA.
Zaharieva, Irina T; Scoto, Mariacristina; Aragon-Gawinska, Karolina; Ridout, Deborah; Doreste, Bruno; Servais, Laurent; Muntoni, Francesco; Zhou, Haiyan.
Afiliação
  • Zaharieva IT; Developmental Neurosciences Research and Teaching Department, Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, University College London, London, UK.
  • Scoto M; Developmental Neurosciences Research and Teaching Department, Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, University College London, London, UK.
  • Aragon-Gawinska K; Great Ormond Street Hospital, London, UK.
  • Ridout D; Institute I-Motion, Hôpital Armand Trousseau, Paris, France.
  • Doreste B; Neurology Department, Medical University of Warsaw, Warsaw, Poland.
  • Servais L; Population, Policy & Practice Department, UCL Great Ormond Street Institute of Child Health, London, UK.
  • Muntoni F; NIHR Great Ormond Street Hospital Biomedical Research Centre, London, UK.
  • Zhou H; Developmental Neurosciences Research and Teaching Department, Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, University College London, London, UK.
Ann Clin Transl Neurol ; 9(7): 1011-1026, 2022 07.
Article em En | MEDLINE | ID: mdl-35584175

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofia Muscular Espinal / MicroRNAs Tipo de estudo: Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limite: Humans / Infant Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofia Muscular Espinal / MicroRNAs Tipo de estudo: Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limite: Humans / Infant Idioma: En Ano de publicação: 2022 Tipo de documento: Article