Developing antisense oligonucleotides for a <i>TECPR2</i> mutation-induced, ultra-rare neurological disorder using patient-derived cellular models.

Williams, Luis A; Gerber, David J; Elder, Amy; Tseng, Wei Chou; Baru, Valeriya; Delaney-Busch, Nathaniel; Ambrosi, Christina; Mahimkar, Gauri; Joshi, Vaibhav; Shah, Himali; Harikrishnan, Karthiayani; Upadhyay, Hansini; Rajendran, Sakthi H; Dhandapani, Aishwarya; Meier, Joshua; Ryan, Steven J; Lewarch, Caitlin; Black, Lauren; Douville, Julie; Cinquino, Stefania; Legakis, Helen; Nalbach, Karsten; Behrends, Christian; Sato, Ai; Galluzzi, Lorenzo; Yu, Timothy W; Brown, Duncan; Agrawal, Sudhir; Margulies, David; Kopin, Alan; Dempsey, Graham T

Developing antisense oligonucleotides for a TECPR2 mutation-induced, ultra-rare neurological disorder using patient-derived cellular models.

Williams, Luis A; Gerber, David J; Elder, Amy; Tseng, Wei Chou; Baru, Valeriya; Delaney-Busch, Nathaniel; Ambrosi, Christina; Mahimkar, Gauri; Joshi, Vaibhav; Shah, Himali; Harikrishnan, Karthiayani; Upadhyay, Hansini; Rajendran, Sakthi H; Dhandapani, Aishwarya; Meier, Joshua; Ryan, Steven J; Lewarch, Caitlin; Black, Lauren; Douville, Julie; Cinquino, Stefania; Legakis, Helen; Nalbach, Karsten; Behrends, Christian; Sato, Ai; Galluzzi, Lorenzo; Yu, Timothy W; Brown, Duncan; Agrawal, Sudhir; Margulies, David; Kopin, Alan; Dempsey, Graham T.

Afiliação

Williams LA; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Gerber DJ; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Elder A; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Tseng WC; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Baru V; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Delaney-Busch N; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Ambrosi C; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Mahimkar G; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Joshi V; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Shah H; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Harikrishnan K; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Upadhyay H; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Rajendran SH; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Dhandapani A; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Meier J; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Ryan SJ; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Lewarch C; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Black L; Charles River Laboratories, Montreal, QC, Canada.
Douville J; Charles River Laboratories, Montreal, QC, Canada.
Cinquino S; Charles River Laboratories, Montreal, QC, Canada.
Legakis H; Charles River Laboratories, Montreal, QC, Canada.
Nalbach K; Munich Cluster for Systems Neurology, Ludwig-Maximilians-Universität München, Germany.
Behrends C; Munich Cluster for Systems Neurology, Ludwig-Maximilians-Universität München, Germany.
Sato A; Department of Radiation Oncology, Weill Cornell Medical College, New York, NY, USA.
Galluzzi L; Department of Radiation Oncology, Weill Cornell Medical College, New York, NY, USA.
Yu TW; Boston Children's Hospital, 300 Longwood Avenue, Boston, MA 02115, USA.
Brown D; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Agrawal S; University of Massachusetts Medical School, Department of Medicine, Worcester, MA 01655, USA.
Margulies D; Arnay Sciences LLC, Shrewsbury, MA 01545, USA.
Kopin A; Q-State Biosciences, 179 Sidney Street, Cambridge, MA 02139, USA.
Dempsey GT; Tufts University School of Medicine, Boston, MA, USA.