Development of an AAV-CRISPR-Cas9-based treatment for dominant cone-rod dystrophy 6.

Mellen, Russell W; Calabro, Kaitlyn R; McCullough, K Tyler; Crosson, Sean M; Cova, Alejandro de la; Fajardo, Diego; Xu, Emily; Boye, Sanford L; Boye, Shannon E

Mellen, Russell W; Calabro, Kaitlyn R; McCullough, K Tyler; Crosson, Sean M; Cova, Alejandro de la; Fajardo, Diego; Xu, Emily; Boye, Sanford L; Boye, Shannon E.

Afiliação

Mellen RW; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
Calabro KR; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
McCullough KT; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
Crosson SM; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
Cova A; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
Fajardo D; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
Xu E; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
Boye SL; Powell Gene Therapy Center, Department of Pediatrics, University of Florida, Gainesville, FL, USA.
Boye SE; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.