Eliminate mitochondrial diseases by gene editing in germ-line cells and embryos
Protein & Cell
; (12): 472-475, 2015.
Article
em En
| WPRIM
| ID: wpr-757219
Biblioteca responsável:
WPRO
ABSTRACT
Nuclease-based gene editing technologies have opened up opportunities for correcting human genetic diseases. For the first time, scientists achieved targeted gene editing of mitochondrial DNA in mouse oocytes fused with patient cells. This fascinating progression may encourage the development of novel therapy for human maternally inherent mitochondrial diseases.
Texto completo:
1
Índice:
WPRIM
Assunto principal:
Terapêutica
/
DNA Mitocondrial
/
Genoma
/
Edição de RNA
/
Doenças Mitocondriais
/
Embrião de Mamíferos
/
Genética
/
Células Germinativas
/
Metabolismo
Limite:
Animals
/
Humans
Idioma:
En
Revista:
Protein & Cell
Ano de publicação:
2015
Tipo de documento:
Article