Rare skin diseases and orphan drugs / 国际药学研究杂志

ABSTRACT

Orphan drugs are medicines or vaccines intended to treat, prevent or diagnose a rare disease. As the number of patients is limited, registration and developmening to enhance the understanding of rare dermatosis and related orphan drugs, this article chooses some presentative diseases in different categories of dermatosis to review, and explains the pathogenesis, therapeutic drugs and related mechanisms.