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1.
Differences in CD80 and CD86 transendocytosis reveal CD86 as a key target for CTLA-4 immune regulation.
Nat Immunol
; 23(9): 1365-1378, 2022 09.
Article
in English
| MEDLINE | ID: mdl-35999394
2.
Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant.
Mol Ther
; 32(6): 1672-1686, 2024 Jun 05.
Article
in English
| MEDLINE | ID: mdl-38549377
3.
Hematopoietic stem cell gene editing rescues B-cell development in X-linked agammaglobulinemia.
J Allergy Clin Immunol
; 2024 Mar 11.
Article
in English
| MEDLINE | ID: mdl-38479630
4.
JAK inhibitor treatment for inborn errors of JAK/STAT signaling: An ESID/EBMT-IEWP retrospective study.
J Allergy Clin Immunol
; 153(1): 275-286.e18, 2024 01.
Article
in English
| MEDLINE | ID: mdl-37935260
5.
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
N Engl J Med
; 384(21): 2002-2013, 2021 05 27.
Article
in English
| MEDLINE | ID: mdl-33974366
6.
Quercetin ameliorates XIAP deficiency-associated hyperinflammation.
Blood
; 140(7): 706-715, 2022 08 18.
Article
in English
| MEDLINE | ID: mdl-35687753
7.
Replication competent retrovirus testing (RCR) in the National Gene Vector Biorepository: No evidence of RCR in 1,595 post-treatment peripheral blood samples obtained from 60 clinical trials.
Mol Ther
; 31(3): 801-809, 2023 03 01.
Article
in English
| MEDLINE | ID: mdl-36518078
8.
Ultrasonographic, endoscopic and radiographic examinations of the dromedary mammary glands and teats.
Trop Anim Health Prod
; 56(5): 180, 2024 May 31.
Article
in English
| MEDLINE | ID: mdl-38819754
9.
Lentiviral Gene Transfer Corrects Immune Abnormalities in XIAP Deficiency.
J Clin Immunol
; 43(2): 440-451, 2023 02.
Article
in English
| MEDLINE | ID: mdl-36329240
10.
Non-osteopenic Bone Pathology After Allo-hematopoietic Stem Cell Transplantation in Patients with Inborn Errors of Immunity.
J Clin Immunol
; 43(5): 1019-1031, 2023 07.
Article
in English
| MEDLINE | ID: mdl-36930409
11.
Absent B cells, agammaglobulinemia, and hypertrophic cardiomyopathy in folliculin-interacting protein 1 deficiency.
Blood
; 137(4): 493-499, 2021 01 28.
Article
in English
| MEDLINE | ID: mdl-32905580
12.
Allosteric inhibition of SHP2 rescues functional T-cell abnormalities in SAP deficiency.
J Allergy Clin Immunol
; 150(6): 1507-1516.e7, 2022 12.
Article
in English
| MEDLINE | ID: mdl-35839843
13.
Phenotype, genotype, treatment, and survival outcomes in patients with X-linked inhibitor of apoptosis deficiency.
J Allergy Clin Immunol
; 150(2): 456-466, 2022 08.
Article
in English
| MEDLINE | ID: mdl-34920033
14.
Preemptive hematopoietic cell transplantation for asymptomatic patients with X-linked lymphoproliferative syndrome type 1.
Clin Immunol
; 237: 108993, 2022 04.
Article
in English
| MEDLINE | ID: mdl-35367395
15.
Patients with XLP type 1 have variable numbers of NKT cells.
Br J Haematol
; 198(1): 151-154, 2022 07.
Article
in English
| MEDLINE | ID: mdl-35355252
16.
Long-Term Immune Recovery After Hematopoietic Stem Cell Transplantation for ADA Deficiency: a Single-Center Experience.
J Clin Immunol
; 42(1): 94-107, 2022 01.
Article
in English
| MEDLINE | ID: mdl-34654999
17.
Retrospective, Landmark Analysis of Long-term Adult Morbidity Following Allogeneic HSCT for Inborn Errors of Immunity in Infancy and Childhood.
J Clin Immunol
; 42(6): 1230-1243, 2022 08.
Article
in English
| MEDLINE | ID: mdl-35579633
18.
Reduced-Intensity/Reduced-Toxicity Conditioning Approaches Are Tolerated in XIAP Deficiency but Patients Fare Poorly with Acute GVHD.
J Clin Immunol
; 42(1): 36-45, 2022 01.
Article
in English
| MEDLINE | ID: mdl-34586554
19.
Gene therapy for primary immunodeficiency.
Hum Mol Genet
; 28(R1): R15-R23, 2019 10 01.
Article
in English
| MEDLINE | ID: mdl-31297531
20.
Gene therapy for primary immunodeficiencies.
Br J Haematol
; 193(6): 1044-1059, 2021 06.
Article
in English
| MEDLINE | ID: mdl-33336808