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1.
AAV-mediated gene therapy for sialidosis.
Mol Ther
; 2024 May 25.
Article
in English
| MEDLINE | ID: mdl-38796704
2.
Altered GM1 catabolism affects NMDAR-mediated Ca2+ signaling at ER-PM junctions and increases synaptic spine formation in a GM1-gangliosidosis model.
Cell Rep
; 43(5): 114117, 2024 May 28.
Article
in English
| MEDLINE | ID: mdl-38630590
3.
AAV-mediated gene therapy for Sialidosis.
bioRxiv
; 2023 Nov 13.
Article
in English
| MEDLINE | ID: mdl-38014061
4.
Altered GM1 catabolism affects NMDAR-mediated Ca 2+ signaling at ER-PM junctions and increases synaptic spine formation.
bioRxiv
; 2023 Jul 11.
Article
in English
| MEDLINE | ID: mdl-37503265
5.
AAV-mediated gene therapy for galactosialidosis: A long-term safety and efficacy study.
Mol Ther Methods Clin Dev
; 23: 644-658, 2021 Dec 10.
Article
in English
| MEDLINE | ID: mdl-34901309
6.
Conventional and Unconventional Therapeutic Strategies for Sialidosis Type I.
J Clin Med
; 9(3)2020 03 04.
Article
in English
| MEDLINE | ID: mdl-32143456
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