Search details
1.
Exploring the relationship between softness and excess entropy in glass-forming systems.
J Chem Phys
; 158(20)2023 May 28.
Article
in English
| MEDLINE | ID: mdl-37218701
2.
Chronic systemic therapy with low-dose morpholino oligomers ameliorates the pathology and normalizes locomotor behavior in mdx mice.
Mol Ther
; 19(2): 345-54, 2011 Feb.
Article
in English
| MEDLINE | ID: mdl-21102560
3.
Transcriptomic analysis of dystrophin RNAi knockdown reveals a central role for dystrophin in muscle differentiation and contractile apparatus organization.
BMC Genomics
; 11: 345, 2010 Jun 01.
Article
in English
| MEDLINE | ID: mdl-20515474
4.
RNAi-mediated knockdown of dystrophin expression in adult mice does not lead to overt muscular dystrophy pathology.
Hum Mol Genet
; 17(17): 2622-32, 2008 Sep 01.
Article
in English
| MEDLINE | ID: mdl-18511456
5.
Design of phosphorodiamidate morpholino oligomers (PMOs) for the induction of exon skipping of the human DMD gene.
Mol Ther
; 17(3): 554-61, 2009 Mar.
Article
in English
| MEDLINE | ID: mdl-19142179
6.
Codon and mRNA sequence optimization of microdystrophin transgenes improves expression and physiological outcome in dystrophic mdx mice following AAV2/8 gene transfer.
Mol Ther
; 16(11): 1825-32, 2008 Nov.
Article
in English
| MEDLINE | ID: mdl-18766174
7.
Efficient liver-directed gene transfer by in situ generation of retroviral vector from adenoviral templates.
In Vivo
; 23(6): 885-93, 2009.
Article
in English
| MEDLINE | ID: mdl-20023229
8.
Apolipoprotein E delivery by peritoneal implantation of encapsulated recombinant cells improves the hyperlipidaemic profile in apoE-deficient mice.
Biochim Biophys Acta
; 1686(3): 190-9, 2005 Jan 05.
Article
in English
| MEDLINE | ID: mdl-15629688
9.
Gene repair and mutagenesis mediated by chimeric RNA-DNA oligonucleotides: chimeraplasty for gene therapy and conversion of single nucleotide polymorphisms (SNPs).
Biochim Biophys Acta
; 1587(1): 1-6, 2002 May 21.
Article
in English
| MEDLINE | ID: mdl-12009417
10.
A risk-based approach to reducing exposure of staff to laboratory animal allergens.
Lab Anim (NY)
; 44(1): 32-8, 2015 Jan.
Article
in English
| MEDLINE | ID: mdl-25526057
11.
Bioinformatic and functional optimization of antisense phosphorodiamidate morpholino oligomers (PMOs) for therapeutic modulation of RNA splicing in muscle.
Methods Mol Biol
; 709: 153-78, 2011.
Article
in English
| MEDLINE | ID: mdl-21194027
12.
Adeno-associated virus serotypes 7 and 8 outperform serotype 9 in expressing atheroprotective human apoE3 from mouse skeletal muscle.
Metabolism
; 60(4): 491-8, 2011 Apr.
Article
in English
| MEDLINE | ID: mdl-20580777
13.
Comparative analysis of antisense oligonucleotide sequences targeting exon 53 of the human DMD gene: Implications for future clinical trials.
Neuromuscul Disord
; 20(2): 102-10, 2010 Feb.
Article
in English
| MEDLINE | ID: mdl-20079639
14.
Dosing regimen has a significant impact on the efficiency of morpholino oligomer-induced exon skipping in mdx mice.
Hum Gene Ther
; 20(9): 955-65, 2009 Sep.
Article
in English
| MEDLINE | ID: mdl-19469709
15.
Preliminary evaluation of a self-complementary AAV2/8 vector for hepatic gene transfer of human apoE3 to inhibit atherosclerotic lesion development in apoE-deficient mice.
Atherosclerosis
; 204(1): 121-6, 2009 May.
Article
in English
| MEDLINE | ID: mdl-18930458
16.
Adeno-associated virus-8-mediated intravenous transfer of myostatin propeptide leads to systemic functional improvements of slow but not fast muscle.
Rejuvenation Res
; 12(2): 85-94, 2009 Apr.
Article
in English
| MEDLINE | ID: mdl-19405813
17.
Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study.
Lancet Neurol
; 8(10): 918-28, 2009 Oct.
Article
in English
| MEDLINE | ID: mdl-19713152
18.
Human apolipoprotein E expression from mouse skeletal muscle by electrotransfer of nonviral DNA (plasmid) and pseudotyped recombinant adeno-associated virus (AAV2/7).
Hum Gene Ther
; 19(6): 569-78, 2008 Jun.
Article
in English
| MEDLINE | ID: mdl-18578629
19.
Adenovirus-based targeting in myoblasts is hampered by nonhomologous vector integration.
Hum Gene Ther
; 19(10): 1000-8, 2008 Oct.
Article
in English
| MEDLINE | ID: mdl-18788904
20.
Towards a therapeutic inhibition of dystrophin exon 23 splicing in mdx mouse muscle induced by antisense oligoribonucleotides (splicomers): target sequence optimisation using oligonucleotide arrays.
J Gene Med
; 6(10): 1149-58, 2004 Oct.
Article
in English
| MEDLINE | ID: mdl-15386737