SMN2 splice modulators enhance U1-pre-mRNA association and rescue SMA mice.
Nat Chem Biol
; 11(7): 511-7, 2015 Jul.
Article
in En
| MEDLINE
| ID: mdl-26030728
Full text:
1
Database:
MEDLINE
Main subject:
RNA, Double-Stranded
/
Muscular Atrophy, Spinal
/
Ribonucleoprotein, U1 Small Nuclear
/
Alternative Splicing
/
Small Molecule Libraries
/
Survival of Motor Neuron 2 Protein
Type of study:
Risk_factors_studies
Limits:
Animals
/
Female
/
Humans
Language:
En
Year:
2015
Type:
Article