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Building global development strategies for cf therapeutics during a transitional cftr modulator era.
Mayer-Hamblett, N; van Koningsbruggen-Rietschel, S; Nichols, D P; VanDevanter, D R; Davies, J C; Lee, T; Durmowicz, A G; Ratjen, F; Konstan, M W; Pearson, K; Bell, S C; Clancy, J P; Taylor-Cousar, J L; De Boeck, K; Donaldson, S H; Downey, D G; Flume, P A; Drevinek, P; Goss, C H; Fajac, I; Magaret, A S; Quon, B S; Singleton, S M; VanDalfsen, J M; Retsch-Bogart, G Z.
Affiliation
  • Mayer-Hamblett N; University of Washington, Seattle, WA; Seattle Children's Hospital, Seattle, WA. Electronic address: nicole.hamblett@seattlechildrens.org.
  • van Koningsbruggen-Rietschel S; Cystic Fibrosis Center, Children's Hospital, University of Cologne; Faculty of Medicine and University Hospital Cologne, Cologne Germany.
  • Nichols DP; University of Washington, Seattle, WA; Seattle Children's Hospital, Seattle, WA.
  • VanDevanter DR; Case Western Reserve University School of Medicine, Cleveland, OH.
  • Davies JC; National Heart & Lung Institute, Imperial College London, London, UK; Royal Brompton & Harefield NHS Foundation Trust, London, UK.
  • Lee T; Leeds Regional Paediatric Cystic Fibrosis Centre, Leeds, UK.
  • Durmowicz AG; Cystic Fibrosis Foundation, Bethesda, MD.
  • Ratjen F; University of Toronto, Toronto, Canada.
  • Konstan MW; Case Western Reserve University School of Medicine, Cleveland, OH; Rainbow Babies and Children's Hospital, Cleveland, OH.
  • Pearson K; Seattle Children's Hospital, Seattle, WA.
  • Bell SC; Children's Health Research Centre, The University of Queensland, Brisbane, Australia.
  • Clancy JP; Cystic Fibrosis Foundation, Bethesda, MD.
  • Taylor-Cousar JL; National Jewish Health, Denver, CO.
  • De Boeck K; University of Leuven, Leuven, Belgium.
  • Donaldson SH; University of North Carolina at Chapel Hill, Chapel Hill, NC.
  • Downey DG; Centre for Experimental Medicine, Queen's University Belfast, Belfast, Northern Ireland.
  • Flume PA; Medical University of South Carolina, Charleston, SC.
  • Drevinek P; Charles University, Prague, Czechia, Motol University Hospital, Prague, Czechia.
  • Goss CH; University of Washington, Seattle, WA; Seattle Children's Hospital, Seattle, WA.
  • Fajac I; Université de Paris, Paris, France.
  • Magaret AS; University of Washington, Seattle, WA; Seattle Children's Hospital, Seattle, WA.
  • Quon BS; University of British Columbia, Vancouver, British Columbia.
  • Singleton SM; Cystic Fibrosis Foundation, Bethesda, MD.
  • VanDalfsen JM; Seattle Children's Hospital, Seattle, WA.
  • Retsch-Bogart GZ; University of North Carolina at Chapel Hill, Chapel Hill, NC.
J Cyst Fibros ; 19(5): 677-687, 2020 09.
Article in En | MEDLINE | ID: mdl-32522463

Full text: 1 Database: MEDLINE Main subject: Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Drug Development / International Cooperation Type of study: Clinical_trials Limits: Humans Language: En Year: 2020 Type: Article

Full text: 1 Database: MEDLINE Main subject: Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Drug Development / International Cooperation Type of study: Clinical_trials Limits: Humans Language: En Year: 2020 Type: Article