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Non-uniform dystrophin re-expression after CRISPR-mediated exon excision in the dystrophin/utrophin double-knockout mouse model of DMD.
Hanson, Britt; Stenler, Sofia; Ahlskog, Nina; Chwalenia, Katarzyna; Svrzikapa, Nenad; Coenen-Stass, Anna M L; Weinberg, Marc S; Wood, Matthew J A; Roberts, Thomas C.
Affiliation
  • Hanson B; Department of Paediatrics, University of Oxford, South Parks Road, Oxford OX1 3QX, UK.
  • Stenler S; Department of Physiology, Anatomy and Genetics, University of Oxford, South Parks Road, Oxford OX1 3QX, UK.
  • Ahlskog N; Department of Physiology, Anatomy and Genetics, University of Oxford, South Parks Road, Oxford OX1 3QX, UK.
  • Chwalenia K; Department of Paediatrics, University of Oxford, South Parks Road, Oxford OX1 3QX, UK.
  • Svrzikapa N; Institute of Developmental and Regenerative Medicine, University of Oxford, IMS-Tetsuya Nakamura Building, Old Road Campus, Roosevelt Dr, Headington, Oxford OX3 7TY, UK.
  • Coenen-Stass AML; Department of Paediatrics, University of Oxford, South Parks Road, Oxford OX1 3QX, UK.
  • Weinberg MS; Institute of Developmental and Regenerative Medicine, University of Oxford, IMS-Tetsuya Nakamura Building, Old Road Campus, Roosevelt Dr, Headington, Oxford OX3 7TY, UK.
  • Wood MJA; Department of Paediatrics, University of Oxford, South Parks Road, Oxford OX1 3QX, UK.
  • Roberts TC; Institute of Developmental and Regenerative Medicine, University of Oxford, IMS-Tetsuya Nakamura Building, Old Road Campus, Roosevelt Dr, Headington, Oxford OX3 7TY, UK.
Mol Ther Nucleic Acids ; 30: 379-397, 2022 Dec 13.
Article in En | MEDLINE | ID: mdl-36420212