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GAA deficiency disrupts distal airway cells in Pompe disease.
El Haddad, Léa; Lai, Elias; Murthy, Preetish Kadur Lakshminarasimha; Biswas, Debolina D; Soufny, Rania; Roger, Angela L; Tata, Purushothama Rao; ElMallah, Mai K.
Affiliation
  • El Haddad L; Division of Pulmonary and Sleep Medicine, Department of Pediatrics, School of Medicine, Duke University, Durham, North Carolina, United States.
  • Lai E; Division of Pulmonary and Sleep Medicine, Department of Pediatrics, School of Medicine, Duke University, Durham, North Carolina, United States.
  • Murthy PKL; Department of Cell Biology, Duke University, Durham, North Carolina, United States.
  • Biswas DD; Division of Pulmonary and Sleep Medicine, Department of Pediatrics, School of Medicine, Duke University, Durham, North Carolina, United States.
  • Soufny R; Division of Pulmonary and Sleep Medicine, Department of Pediatrics, School of Medicine, Duke University, Durham, North Carolina, United States.
  • Roger AL; Division of Pulmonary and Sleep Medicine, Department of Pediatrics, School of Medicine, Duke University, Durham, North Carolina, United States.
  • Tata PR; Department of Cell Biology, Duke University, Durham, North Carolina, United States.
  • ElMallah MK; Division of Pulmonary and Sleep Medicine, Department of Pediatrics, School of Medicine, Duke University, Durham, North Carolina, United States.
Am J Physiol Lung Cell Mol Physiol ; 325(3): L288-L298, 2023 09 01.
Article in En | MEDLINE | ID: mdl-37366541

Full text: 1 Database: MEDLINE Main subject: Respiratory Insufficiency / Glycogen Storage Disease Type II Type of study: Prognostic_studies Limits: Humans Language: En Year: 2023 Type: Article

Full text: 1 Database: MEDLINE Main subject: Respiratory Insufficiency / Glycogen Storage Disease Type II Type of study: Prognostic_studies Limits: Humans Language: En Year: 2023 Type: Article