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Antisense Oligonucleotide-Based Therapy for Neuromuscular Disease.
Sardone, Valentina; Zhou, Haiyan; Muntoni, Francesco; Ferlini, Alessandra; Falzarano, Maria Sofia.
Afiliación
  • Sardone V; Dubowitz Neuromuscular Centre, Molecular Neurosciences Section, Developmental Neuroscience Programme, UCL Great Ormond Street Institute of Child Health, London WC1N 1EH, UK. v.sardone@ucl.ac.uk.
  • Zhou H; Dubowitz Neuromuscular Centre, Molecular Neurosciences Section, Developmental Neuroscience Programme, UCL Great Ormond Street Institute of Child Health, London WC1N 1EH, UK. haiyan.zhou@ucl.ac.uk.
  • Muntoni F; Dubowitz Neuromuscular Centre, Molecular Neurosciences Section, Developmental Neuroscience Programme, UCL Great Ormond Street Institute of Child Health, London WC1N 1EH, UK. f.muntoni@ucl.ac.uk.
  • Ferlini A; MRC Centre for Neuromuscular Diseases, UCL Institute of Neurology, London WC1N 3BG, UK. f.muntoni@ucl.ac.uk.
  • Falzarano MS; Dubowitz Neuromuscular Centre, Molecular Neurosciences Section, Developmental Neuroscience Programme, UCL Great Ormond Street Institute of Child Health, London WC1N 1EH, UK. fla@unife.it.
Molecules ; 22(4)2017 Apr 05.
Article en En | MEDLINE | ID: mdl-28379182

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Terapia Genética / Oligonucleótidos Antisentido / Enfermedades Neuromusculares Tipo de estudio: Diagnostic_studies / Prognostic_studies Límite: Animals / Humans Idioma: En Año: 2017 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Terapia Genética / Oligonucleótidos Antisentido / Enfermedades Neuromusculares Tipo de estudio: Diagnostic_studies / Prognostic_studies Límite: Animals / Humans Idioma: En Año: 2017 Tipo del documento: Article