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Effects of enzyme replacement therapy on bone density in late onset Pompe disease.
Avanti, Mahima; Martin, Angela; Columbres, Rod Carlo; Mozaffar, Tahseen; Kimonis, Virginia.
Afiliación
  • Avanti M; Division of Genetics, Department of Pediatrics, University of California - Irvine, Orange, CA 92697, United States of America.
  • Martin A; Division of Genetics, Department of Pediatrics, University of California - Irvine, Orange, CA 92697, United States of America.
  • Columbres RC; Division of Genetics, Department of Pediatrics, University of California - Irvine, Orange, CA 92697, United States of America.
  • Mozaffar T; Division of Neuromuscular Diseases, Department of Neurology, University of California- Irvine, 200 S. Manchester Ave., Suite 206, Orange, CA, United States of America.
  • Kimonis V; Division of Genetics, Department of Pediatrics, University of California - Irvine, Orange, CA 92697, United States of America; Division of Neuromuscular Diseases, Department of Neurology, University of California- Irvine, 200 S. Manchester Ave., Suite 206, Orange, CA, United States of America; Depar
Mol Genet Metab ; 140(3): 107644, 2023 11.
Article en En | MEDLINE | ID: mdl-37515933

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Osteoporosis / Enfermedad del Almacenamiento de Glucógeno Tipo II Tipo de estudio: Guideline Límite: Female / Humans / Male Idioma: En Año: 2023 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Osteoporosis / Enfermedad del Almacenamiento de Glucógeno Tipo II Tipo de estudio: Guideline Límite: Female / Humans / Male Idioma: En Año: 2023 Tipo del documento: Article