The DcpS inhibitor RG3039 improves survival, function and motor unit pathologies in two SMA mouse models.
Hum Mol Genet
; 22(20): 4084-101, 2013 Oct 15.
Article
in En
| MEDLINE
| ID: mdl-23736298
Full text:
1
Database:
MEDLINE
Main subject:
Quinazolines
/
Muscular Atrophy, Spinal
/
Endoribonucleases
/
Survival of Motor Neuron 2 Protein
/
Motor Neurons
Language:
En
Journal:
Hum Mol Genet
Year:
2013
Type:
Article