Long term follow-up to evaluate the efficacy of miglustat treatment in Italian patients with Niemann-Pick disease type C.
Orphanet J Rare Dis
; 10: 22, 2015 Feb 27.
Article
in En
| MEDLINE
| ID: mdl-25888393
Full text:
1
Database:
MEDLINE
Therapeutic Methods and Therapies TCIM:
Terapias_biologicas
/
Aromoterapia
Main subject:
1-Deoxynojirimycin
/
Enzyme Inhibitors
/
Niemann-Pick Disease, Type C
Type of study:
Clinical_trials
Country/Region as subject:
Europa
Language:
En
Journal:
Orphanet J Rare Dis
Year:
2015
Type:
Article
Affiliation country:
Italy