Long term outcomes of severe combined immunodeficiency: therapy implications.

Heimall, Jennifer; Cowan, Morton J

Heimall, Jennifer; Cowan, Morton J.

Affiliation

Heimall J; a Allergy/Immunology Attending Physician, Perelman School of Medicine , The Children's Hospital of Philadelphia , Philadelphia , PA , USA.
Cowan MJ; b Allergy Immunology and Blood and Marrow Transplant Division , University of California San Francisco, Benioff Children's Hospital , San Francisco , CA , USA.

Expert Rev Clin Immunol ; 13(11): 1029-1040, 2017 11.

Article in En | MEDLINE | ID: mdl-28918671

Subject(s)

Genotype; Hematopoietic Stem Cell Transplantation; Severe Combined Immunodeficiency/therapy; Expert Testimony; Genetic Therapy; Humans; Infant, Newborn; Neonatal Screening; Severe Combined Immunodeficiency/diagnosis; Severe Combined Immunodeficiency/genetics; Transplantation Conditioning; Treatment Outcome

Key words

Hematopoietic Stem Cell Transplant (HCT); Newborn Screening (NBS); RAG SCID; Radiosensitive SCID (RS-SCID); Severe Combined Immunodeficiency (SCID); TREC; XSCID; conditioning; gene therapy; late effects

Fulltext

Add to My VHL

XML

PubMed Links

Search on Google

Full text: 1 Database: MEDLINE Main subject: Severe Combined Immunodeficiency / Hematopoietic Stem Cell Transplantation / Genotype Type of study: Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Language: En Journal: Expert Rev Clin Immunol Year: 2017 Type: Article Affiliation country: United States

Fulltext

Add to My VHL

XML

PubMed Links

Search on Google