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Combined miglustat and enzyme replacement therapy in two patients with type 1 Gaucher disease: two case reports.
Amato, Dominick; Patterson, Mary Anne.
Affiliation
  • Amato D; Mount Sinai Hospital, University of Toronto, Toronto, ON, Canada. Dominick.Amato@sinaihealthsystem.ca.
  • Patterson MA; Department of Medicine, Mount Sinai Hospital, 60 Murray Street, Room L-315, Box 34, Toronto, ON, M5G 1X5, Canada. Dominick.Amato@sinaihealthsystem.ca.
J Med Case Rep ; 12(1): 19, 2018 Jan 27.
Article in En | MEDLINE | ID: mdl-29373994

Full text: 1 Database: MEDLINE Therapeutic Methods and Therapies TCIM: Terapias_biologicas / Aromoterapia Main subject: 1-Deoxynojirimycin / Enzyme Inhibitors / Enzyme Replacement Therapy / Gaucher Disease / Glucosylceramidase Type of study: Clinical_trials Language: En Journal: J Med Case Rep Year: 2018 Type: Article Affiliation country: Canada

Full text: 1 Database: MEDLINE Therapeutic Methods and Therapies TCIM: Terapias_biologicas / Aromoterapia Main subject: 1-Deoxynojirimycin / Enzyme Inhibitors / Enzyme Replacement Therapy / Gaucher Disease / Glucosylceramidase Type of study: Clinical_trials Language: En Journal: J Med Case Rep Year: 2018 Type: Article Affiliation country: Canada