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Pharmacologic rescue of an enzyme-trafficking defect in primary hyperoxaluria 1.
Miyata, Non; Steffen, Janos; Johnson, Meghan E; Fargue, Sonia; Danpure, Christopher J; Koehler, Carla M.
Afiliação
  • Miyata N; Department of Chemistry and Biochemistry.
  • Steffen J; Department of Chemistry and Biochemistry.
  • Johnson ME; Department of Chemistry and Biochemistry.
  • Fargue S; Department of Cell and Developmental Biology, Division of Biosciences, University College London, London WC1E 6BT, United Kingdom.
  • Danpure CJ; Department of Cell and Developmental Biology, Division of Biosciences, University College London, London WC1E 6BT, United Kingdom.
  • Koehler CM; Department of Chemistry and Biochemistry, Molecular Biology Institute, and Jonsson Comprehensive Cancer Center, University of California, Los Angeles, CA 90095; and koehler@chem.ucla.edu.
Proc Natl Acad Sci U S A ; 111(40): 14406-11, 2014 Oct 07.
Article em En | MEDLINE | ID: mdl-25237136

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hiperoxalúria Primária / Dequalínio / Transaminases Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2014 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hiperoxalúria Primária / Dequalínio / Transaminases Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2014 Tipo de documento: Article