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The effects of transitioning from immediate release to extended release cysteamine therapy in Norwegian patients with nephropathic cystinosis: a retrospective study.
Bjerre, Anna; Aase, Sonja Amdal; Radtke, Maria; Siva, Christian; Gudmundsdottir, Helga; Forsberg, Brita; Woldseth, Berit; Brackman, Damien.
Afiliação
  • Bjerre A; Department for Specialised Paediatrics, Oslo University Hospital, Oslo, Norway. abjerre@ous-hf.no.
  • Aase SA; Institute of Clinical Medicine, University of Oslo, Oslo, Norway. abjerre@ous-hf.no.
  • Radtke M; Department of Paediatric and Adolescent Medicine, Stavanger University Hospital, Stavanger, Norway.
  • Siva C; Department of Nephrology, St Olav's University Hospital, Trondheim, Norway.
  • Gudmundsdottir H; Department of Clinical and Molecular Medicine, Norwegian University of Science and Technology, Trondheim, Norge.
  • Forsberg B; Paediatric Department, Vestfold Hospital, Tønsberg, Norway.
  • Woldseth B; Nephrology Department, Ullevål, Oslo University Hospital, Oslo, Norway.
  • Brackman D; Chiesi Global Rare Diseases, Nordics, Stockholm, Sweden.
Pediatr Nephrol ; 38(11): 3671-3679, 2023 11.
Article em En | MEDLINE | ID: mdl-37219641

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Cistinose / Síndrome de Fanconi Tipo de estudo: Observational_studies Idioma: En Revista: Pediatr Nephrol Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Noruega

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Cistinose / Síndrome de Fanconi Tipo de estudo: Observational_studies Idioma: En Revista: Pediatr Nephrol Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Noruega