What Can We Learn From Clinical Trials of Exon Skipping for DMD?

Lu, Qi-Long; Cirak, Sebahattin; Partridge, Terence.

Afiliación

Lu QL; Department of Neurology, McColl Lockwood Laboratory for Muscular Dystrophy Research, Carolinas Medical Center, Charlotte, North Carolina, USA.
Cirak S; Center for Genetic Medicine, Children's National Medical Center, NW, Washington, DC, USA.
Partridge T; Center for Genetic Medicine, Children's National Medical Center, NW, Washington, DC, USA.

Mol Ther Nucleic Acids ; 3: e152, 2014 Mar 11.

Article en En | MEDLINE | ID: mdl-24618851

Texto completo: 1 Base de datos: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Año: 2014 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Año: 2014 Tipo del documento: Article