Bioengineered coagulation factor VIII enables long-term correction of murine hemophilia A following liver-directed adeno-associated viral vector delivery.

Brown, Harrison C; Wright, J Fraser; Zhou, Shangzhen; Lytle, Allison M; Shields, Jordan E; Spencer, H Trent; Doering, Christopher B

Brown, Harrison C; Wright, J Fraser; Zhou, Shangzhen; Lytle, Allison M; Shields, Jordan E; Spencer, H Trent; Doering, Christopher B.

Afiliación

Brown HC; Graduate Program in Molecular and Systems Pharmacology, Laney Graduate School, Emory University , Atlanta, Georgia, USA.
Wright JF; Center for Cellular and Molecular Therapeutics, The Children's Hospital of Philadelphia , Philadelphia, Pennsylvania, USA ; Perelman School of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania, USA.
Zhou S; Center for Cellular and Molecular Therapeutics, The Children's Hospital of Philadelphia , Philadelphia, Pennsylvania, USA.
Lytle AM; Graduate Program in Molecular and Systems Pharmacology, Laney Graduate School, Emory University , Atlanta, Georgia, USA.
Shields JE; Department of Pediatrics, Aflac Cancer and Blood Disorders Center, Emory University School of Medicine , Atlanta, Georgia, USA.
Spencer HT; Department of Pediatrics, Aflac Cancer and Blood Disorders Center, Emory University School of Medicine , Atlanta, Georgia, USA.
Doering CB; Department of Pediatrics, Aflac Cancer and Blood Disorders Center, Emory University School of Medicine , Atlanta, Georgia, USA.

Mol Ther Methods Clin Dev ; 1: 14036, 2014.

Article en En | MEDLINE | ID: mdl-26015976

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Texto completo: 1 Base de datos: MEDLINE Tipo de estudio: Risk_factors_studies Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2014 Tipo del documento: Article

Texto completo

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PubMed Links

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Texto completo: 1 Base de datos: MEDLINE Tipo de estudio: Risk_factors_studies Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2014 Tipo del documento: Article