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Triheptanoin versus trioctanoin for long-chain fatty acid oxidation disorders: a double blinded, randomized controlled trial.
Gillingham, Melanie B; Heitner, Stephen B; Martin, Julie; Rose, Sarah; Goldstein, Amy; El-Gharbawy, Areeg Hassan; Deward, Stephanie; Lasarev, Michael R; Pollaro, Jim; DeLany, James P; Burchill, Luke J; Goodpaster, Bret; Shoemaker, James; Matern, Dietrich; Harding, Cary O; Vockley, Jerry.
Afiliación
  • Gillingham MB; Department of Molecular and Medical Genetics, Graduate Programs in Human Nutrition, Oregon Health & Science University, 3181 SW Sam Jackson Park Rd, Portland, OR, 97239, USA. gillingm@ohsu.edu.
  • Heitner SB; Knight Cardiovascular Institute, Oregon Health & Science University, Portland, OR, USA.
  • Martin J; Department of Molecular and Medical Genetics, Graduate Programs in Human Nutrition, Oregon Health & Science University, 3181 SW Sam Jackson Park Rd, Portland, OR, 97239, USA.
  • Rose S; Department of Molecular and Medical Genetics, Graduate Programs in Human Nutrition, Oregon Health & Science University, 3181 SW Sam Jackson Park Rd, Portland, OR, 97239, USA.
  • Goldstein A; PRA Health Sciences, Raleigh, NC, USA.
  • El-Gharbawy AH; Neurogenetics and Metabolism, Children's Hospital of Pittsburgh of UPMC, Pittsburgh, PA, USA.
  • Deward S; Division of Medical Genetics, University of Pittsburgh School of Medicine, Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.
  • Lasarev MR; Division of Medical Genetics, University of Pittsburgh School of Medicine, Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.
  • Pollaro J; GeneDx, Gaithersburg, MD, USA.
  • DeLany JP; Center for Research on Occupational and Environmental Toxicology, Oregon Health & Science University, Portland, OR, USA.
  • Burchill LJ; Advanced Imaging Research Center, Oregon Health & Science University, Portland, OR, USA.
  • Goodpaster B; Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA.
  • Shoemaker J; Knight Cardiovascular Institute, Oregon Health & Science University, Portland, OR, USA.
  • Matern D; Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA.
  • Harding CO; The Florida Hospital Translational Research Institute, and the Sanford Burnham Institute, Orlando, FL, USA.
  • Vockley J; Department of Biochemistry and Molecular Biology, Saint Louis University, Saint Louis, MO, USA.
J Inherit Metab Dis ; 40(6): 831-843, 2017 11.
Article en En | MEDLINE | ID: mdl-28871440

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Rabdomiólisis / Triglicéridos / Caprilatos / Miopatías Mitocondriales / Ácidos Grasos / Proteína Trifuncional Mitocondrial / Errores Innatos del Metabolismo Lipídico / Cardiomiopatías / Enfermedades del Sistema Nervioso Tipo de estudio: Clinical_trials Idioma: En Revista: J Inherit Metab Dis Año: 2017 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Rabdomiólisis / Triglicéridos / Caprilatos / Miopatías Mitocondriales / Ácidos Grasos / Proteína Trifuncional Mitocondrial / Errores Innatos del Metabolismo Lipídico / Cardiomiopatías / Enfermedades del Sistema Nervioso Tipo de estudio: Clinical_trials Idioma: En Revista: J Inherit Metab Dis Año: 2017 Tipo del documento: Article