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Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate.
György, Bence; Meijer, Elise J; Ivanchenko, Maryna V; Tenneson, Kelly; Emond, Frederick; Hanlon, Killian S; Indzhykulian, Artur A; Volak, Adrienn; Karavitaki, K Domenica; Tamvakologos, Panos I; Vezina, Mark; Berezovskii, Vladimir K; Born, Richard T; O'Brien, Maureen; Lafond, Jean-François; Arsenijevic, Yvan; Kenna, Margaret A; Maguire, Casey A; Corey, David P.
Afiliación
  • György B; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Meijer EJ; Molecular Neurogenetics Unit, Massachusetts General Hospital, Harvard Medical School, Charlestown, MA 02114, USA.
  • Ivanchenko MV; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Tenneson K; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Emond F; Charles River Laboratories, Senneville, QC, Canada.
  • Hanlon KS; Charles River Laboratories, Senneville, QC, Canada.
  • Indzhykulian AA; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Volak A; Molecular Neurogenetics Unit, Massachusetts General Hospital, Harvard Medical School, Charlestown, MA 02114, USA.
  • Karavitaki KD; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Tamvakologos PI; Department of Otolaryngology, Massachusetts Eye and Ear, Harvard Medical School, Boston, MA 02114, USA.
  • Vezina M; Molecular Neurogenetics Unit, Massachusetts General Hospital, Harvard Medical School, Charlestown, MA 02114, USA.
  • Berezovskii VK; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Born RT; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • O'Brien M; Charles River Laboratories, Senneville, QC, Canada.
  • Lafond JF; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Arsenijevic Y; Department of Neurobiology, Harvard Medical School, Boston, MA 02115, USA.
  • Kenna MA; Charles River Laboratories, Frederick, MD 21701, USA.
  • Maguire CA; Charles River Laboratories, Senneville, QC, Canada.
  • Corey DP; Unit of Retinal Degeneration and Regeneration, Department of Ophthalmology, University of Lausanne, Jules-Gonin Eye Hospital, Lausanne, Switzerland.
Mol Ther Methods Clin Dev ; 13: 1-13, 2019 Jun 14.
Article en En | MEDLINE | ID: mdl-30581889

Texto completo: 1 Base de datos: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2019 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2019 Tipo del documento: Article