Your browser doesn't support javascript.
loading
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia.
Marktel, Sarah; Scaramuzza, Samantha; Cicalese, Maria Pia; Giglio, Fabio; Galimberti, Stefania; Lidonnici, Maria Rosa; Calbi, Valeria; Assanelli, Andrea; Bernardo, Maria Ester; Rossi, Claudia; Calabria, Andrea; Milani, Raffaella; Gattillo, Salvatore; Benedicenti, Fabrizio; Spinozzi, Giulio; Aprile, Annamaria; Bergami, Alessandra; Casiraghi, Miriam; Consiglieri, Giulia; Masera, Nicoletta; D'Angelo, Emanuela; Mirra, Nadia; Origa, Raffaella; Tartaglione, Immacolata; Perrotta, Silverio; Winter, Robert; Coppola, Milena; Viarengo, Gianluca; Santoleri, Luca; Graziadei, Giovanna; Gabaldo, Michela; Valsecchi, Maria Grazia; Montini, Eugenio; Naldini, Luigi; Cappellini, Maria Domenica; Ciceri, Fabio; Aiuti, Alessandro; Ferrari, Giuliana.
Afiliación
  • Marktel S; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Scaramuzza S; Haematology and BMT Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Cicalese MP; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Giglio F; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Galimberti S; Pediatric Immunohematology, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Lidonnici MR; Haematology and BMT Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Calbi V; Center of Biostatistics for Clinical Epidemiology, School of Medicine and Surgery, University of Milan-Bicocca, Milan, Italy.
  • Assanelli A; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Bernardo ME; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Rossi C; Pediatric Immunohematology, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Calabria A; Haematology and BMT Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Milani R; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Gattillo S; Pediatric Immunohematology, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Benedicenti F; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Spinozzi G; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Aprile A; Blood Transfusion Service, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Bergami A; Blood Transfusion Service, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Casiraghi M; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Consiglieri G; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Masera N; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • D'Angelo E; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Mirra N; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Origa R; Pediatric Immunohematology, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Tartaglione I; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Perrotta S; Pediatric Immunohematology, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Winter R; Pediatric Department University of Milano-Bicocca, San Gerardo Hospital, Monza, Italy.
  • Coppola M; Pediatric Clinic/DH, Fondazione IRCCS Ca' Granda, Milan, Italy.
  • Viarengo G; Pediatric Clinic/DH, Fondazione IRCCS Ca' Granda, Milan, Italy.
  • Santoleri L; Ospedale Pediatrico Microcitemico "A.Cao", A.O. "G.Brotzu", Cagliari, Italy.
  • Graziadei G; Department of Woman, Child and General and Specialist Surgery, Università degli studi della Campania "Luigi Vanvitelli", Napoli, Italy.
  • Gabaldo M; Department of Woman, Child and General and Specialist Surgery, Università degli studi della Campania "Luigi Vanvitelli", Napoli, Italy.
  • Valsecchi MG; Department of Chemical Pathology, Great Ormond Street Hospital NHS Foundation Trust, London, UK.
  • Montini E; Blood Transfusion Service, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Naldini L; Immunohematology and Transfusion Medicine Service, Fondazione IRCCS Policlinico S. Matteo, Pavia, Italy.
  • Cappellini MD; Blood Transfusion Service, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Ciceri F; Rare Disease Center, Fondazione IRCCS Ca' Granda, University of Milan, Milan, Italy.
  • Aiuti A; San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Ferrari G; Center of Biostatistics for Clinical Epidemiology, School of Medicine and Surgery, University of Milan-Bicocca, Milan, Italy.
Nat Med ; 25(2): 234-241, 2019 02.
Article en En | MEDLINE | ID: mdl-30664781
Asunto(s)
Texto completo
Imprimir
XML
PubMed Links
Buscar en Google

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Transfusión Sanguínea / Huesos / Células Madre Hematopoyéticas / Terapia Genética / Talasemia beta / Trasplante de Células Madre Hematopoyéticas Idioma: En Revista: Nat Med Asunto de la revista: BIOLOGIA MOLECULAR / MEDICINA Año: 2019 Tipo del documento: Article
Texto completo
Imprimir
XML
PubMed Links
Buscar en Google

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Transfusión Sanguínea / Huesos / Células Madre Hematopoyéticas / Terapia Genética / Talasemia beta / Trasplante de Células Madre Hematopoyéticas Idioma: En Revista: Nat Med Asunto de la revista: BIOLOGIA MOLECULAR / MEDICINA Año: 2019 Tipo del documento: Article