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Agalsidase beta treatment slows estimated glomerular filtration rate loss in classic Fabry disease patients: results from an individual patient data meta-analysis.
Ortiz, Alberto; Kanters, Steve; Hamed, Alaa; DasMahapatra, Pronabesh; Poggio, Eugene; Maski, Manish; Aguiar, Mario; Ponce, Elvira; Jansen, Jeroen P; Ayers, Dieter; Goldgrub, Rachel; Desnick, Robert J.
Afiliación
  • Ortiz A; Unidad de Diálisis, IIS-Fundación Jiménez Díaz, School of Medicine, UAM, IRSIN and REDINREN, Madrid, Spain.
  • Kanters S; Evidence Synthesis and Decision Modeling, Precision HEOR, Vancouver, BC, Canada.
  • Hamed A; Sanofi Genzyme Health Economics and Value Assessment, Genzyme, Cambridge, MA, USA.
  • DasMahapatra P; Sanofi Genzyme Health Economics and Value Assessment, Genzyme, Cambridge, MA, USA.
  • Poggio E; Biostatistical Consulting Inc., Lexington, MA, USA.
  • Maski M; Sanofi Genzyme Medical Affairs, Genzyme, Cambridge, MA, USA.
  • Aguiar M; Sanofi Genzyme Medical Affairs, Genzyme, Cambridge, MA, USA.
  • Ponce E; Sanofi Genzyme Medical Affairs, Genzyme, Cambridge, MA, USA.
  • Jansen JP; Evidence Synthesis and Decision Modeling, Precision HEOR, Oakland, CA, USA.
  • Ayers D; Evidence Synthesis and Decision Modeling, Precision HEOR, Vancouver, BC, Canada.
  • Goldgrub R; Evidence Synthesis and Decision Modeling, Precision HEOR, Vancouver, BC, Canada.
  • Desnick RJ; Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, USA.
Clin Kidney J ; 14(4): 1136-1146, 2021 Apr.
Article en En | MEDLINE | ID: mdl-33841859

Texto completo: 1 Base de datos: MEDLINE Tipo de estudio: Prognostic_studies / Systematic_reviews Idioma: En Revista: Clin Kidney J Año: 2021 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Tipo de estudio: Prognostic_studies / Systematic_reviews Idioma: En Revista: Clin Kidney J Año: 2021 Tipo del documento: Article