Effective gene therapy of Stargardt disease with PEG-ECO/<i>pGRK1-ABCA4-S/MAR</i> nanoparticles.

Sun, Da; Sun, Wenyu; Gao, Song-Qi; Lehrer, Jonathan; Naderi, Amirreza; Wei, Cheng; Lee, Sangjoon; Schilb, Andrew L; Scheidt, Josef; Hall, Ryan C; Traboulsi, Elias I; Palczewski, Krzysztof; Lu, Zheng-Rong

Effective gene therapy of Stargardt disease with PEG-ECO/pGRK1-ABCA4-S/MAR nanoparticles.

Sun, Da; Sun, Wenyu; Gao, Song-Qi; Lehrer, Jonathan; Naderi, Amirreza; Wei, Cheng; Lee, Sangjoon; Schilb, Andrew L; Scheidt, Josef; Hall, Ryan C; Traboulsi, Elias I; Palczewski, Krzysztof; Lu, Zheng-Rong.

Afiliación

Sun D; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Sun W; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Gao SQ; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Lehrer J; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Naderi A; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Wei C; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Lee S; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Schilb AL; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Scheidt J; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Hall RC; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.
Traboulsi EI; Department of Pediatric Ophthalmology and Center for Genetic Eye Diseases, Cole Eye Institute, Cleveland Clinic, 9500 Euclid Avenue, Cleveland, OH 44106, USA.
Palczewski K; Gavin Herbert Eye Institute, Department of Ophthalmology, Departments of Physiology and Biophysics, Chemistry, and Molecular Biology and Biochemistry, University of California Irvine, Irvine, CA 92697, USA.
Lu ZR; Department of Biomedical Engineering, Case Western Reserve University, 10900 Euclid Avenue, Cleveland, OH 44106, USA.