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Sex-split analysis of pathology and motor-behavioral outcomes in a mouse model of CLN8-Batten disease reveals an increased disease burden and trajectory in female Cln8mnd mice.
Holmes, Andrew D; White, Katherine A; Pratt, Melissa A; Johnson, Tyler B; Likhite, Shibi; Meyer, Kathrin; Weimer, Jill M.
Afiliación
  • Holmes AD; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E 60Th St N, Sioux Falls, SD, USA.
  • White KA; Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Sioux Falls, SD, USA.
  • Pratt MA; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E 60Th St N, Sioux Falls, SD, USA.
  • Johnson TB; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E 60Th St N, Sioux Falls, SD, USA.
  • Likhite S; Pediatrics and Rare Diseases Group, Sanford Research, 2301 E 60Th St N, Sioux Falls, SD, USA.
  • Meyer K; The Research Institute at Nationwide Children's Hospital, Columbus, OH, USA.
  • Weimer JM; The Research Institute at Nationwide Children's Hospital, Columbus, OH, USA.
Orphanet J Rare Dis ; 17(1): 411, 2022 11 11.
Article en En | MEDLINE | ID: mdl-36369162

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Lipofuscinosis Ceroideas Neuronales Tipo de estudio: Prognostic_studies Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2022 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Lipofuscinosis Ceroideas Neuronales Tipo de estudio: Prognostic_studies Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2022 Tipo del documento: Article