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Efficacy confirmation study of aceneuramic acid administration for GNE myopathy in Japan.
Mori-Yoshimura, Madoka; Suzuki, Naoki; Katsuno, Masahisa; Takahashi, Masanori P; Yamashita, Satoshi; Oya, Yasushi; Hashizume, Atsushi; Yamada, Shinichiro; Nakamori, Masayuki; Izumi, Rumiko; Kato, Masaaki; Warita, Hitoshi; Tateyama, Maki; Kuroda, Hiroshi; Asada, Ryuta; Yamaguchi, Takuhiro; Nishino, Ichizo; Aoki, Masashi.
Afiliación
  • Mori-Yoshimura M; Department of Neurology, National Center Hospital, National Center of Neurology and Psychiatry (NCNP), Tokyo, Japan.
  • Suzuki N; Department of Neurology, Tohoku University Graduate School of Medicine, 1-1 Seiryo-Machi, Aoba-Ku, Sendai, 980-8574, Japan.
  • Katsuno M; Department of Neurology, Nagoya University Graduate School of Medicine, Nagoya, Japan.
  • Takahashi MP; Department of Clinical Research Education, Nagoya University Graduate School of Medicine, Nagoya, Japan.
  • Yamashita S; Department of Neurology, Osaka University Hospital, Osaka, Japan.
  • Oya Y; Department of Neurology, Kumamoto University Hospital, Kumamoto, Japan.
  • Hashizume A; Department of Neurology, National Center Hospital, National Center of Neurology and Psychiatry (NCNP), Tokyo, Japan.
  • Yamada S; Department of Neurology, Nagoya University Graduate School of Medicine, Nagoya, Japan.
  • Nakamori M; Department of Clinical Research Education, Nagoya University Graduate School of Medicine, Nagoya, Japan.
  • Izumi R; Department of Neurology, Nagoya University Graduate School of Medicine, Nagoya, Japan.
  • Kato M; Department of Neurology, Osaka University Hospital, Osaka, Japan.
  • Warita H; Department of Neurology, Tohoku University Graduate School of Medicine, 1-1 Seiryo-Machi, Aoba-Ku, Sendai, 980-8574, Japan.
  • Tateyama M; Department of Neurology, Tohoku University Graduate School of Medicine, 1-1 Seiryo-Machi, Aoba-Ku, Sendai, 980-8574, Japan.
  • Kuroda H; Department of Neurology, Tohoku University Graduate School of Medicine, 1-1 Seiryo-Machi, Aoba-Ku, Sendai, 980-8574, Japan.
  • Asada R; Department of Neurology, Tohoku University Graduate School of Medicine, 1-1 Seiryo-Machi, Aoba-Ku, Sendai, 980-8574, Japan.
  • Yamaguchi T; Department of Neurology, Tohoku University Graduate School of Medicine, 1-1 Seiryo-Machi, Aoba-Ku, Sendai, 980-8574, Japan.
  • Nishino I; Innovative and Clinical Research Promotion Center, Gifu University Hospital, Gifu, Japan.
  • Aoki M; Division of Biostatistics, Tohoku University Graduate School of Medicine, Sendai, Japan.
Orphanet J Rare Dis ; 18(1): 241, 2023 08 11.
Article en En | MEDLINE | ID: mdl-37568154

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Ácido N-Acetilneuramínico / Miopatías Distales Tipo de estudio: Clinical_trials País/Región como asunto: Asia Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2023 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Ácido N-Acetilneuramínico / Miopatías Distales Tipo de estudio: Clinical_trials País/Región como asunto: Asia Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2023 Tipo del documento: Article