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Preclinical Development and Characterization of Novel Adeno-Associated Viral Vectors for the Treatment of Lipoprotein Lipase Deficiency.
Mehta, Neel; Gilbert, Rénald; Chahal, Parminder S; Moreno, Maria J; Nassoury, Nasha; Coulombe, Nathalie; Lytvyn, Viktoria; Mercier, Mario; Fatehi, Dorothy; Lin, Wendy; Harvey, Emily M; Zhang, Lin-Hua; Nazemi-Moghaddam, Nazila; Elahi, Seyyed Mehdy; Ross, Colin J D; Stanimirovic, Danica B; Hayden, Michael R.
Afiliación
  • Mehta N; Department of Medical Genetics, Center for Molecular Medicine and Therapeutics, BC Children's Hospital Research Institute, University of British Columbia, Vancouver, Canada.
  • Gilbert R; Department of Production Platforms and Analytics, Human Health Therapeutics Research Center, National Research Council Canada, Montréal, Canada.
  • Chahal PS; Department of Bioengineering, McGill University, Montréal, Canada.
  • Moreno MJ; Department of Production Platforms and Analytics, Human Health Therapeutics Research Center, National Research Council Canada, Montréal, Canada.
  • Nassoury N; Department of Translational Biosciences, Human Health Therapeutics Research Center, National Research Council Canada, Ottawa, Canada.
  • Coulombe N; Department of Production Platforms and Analytics, Human Health Therapeutics Research Center, National Research Council Canada, Montréal, Canada.
  • Lytvyn V; Department of Production Platforms and Analytics, Human Health Therapeutics Research Center, National Research Council Canada, Montréal, Canada.
  • Mercier M; Department of Production Platforms and Analytics, Human Health Therapeutics Research Center, National Research Council Canada, Montréal, Canada.
  • Fatehi D; Department of Translational Biosciences, Human Health Therapeutics Research Center, National Research Council Canada, Ottawa, Canada.
  • Lin W; Department of Translational Biosciences, Human Health Therapeutics Research Center, National Research Council Canada, Ottawa, Canada.
  • Harvey EM; Department of Medical Genetics, Center for Molecular Medicine and Therapeutics, BC Children's Hospital Research Institute, University of British Columbia, Vancouver, Canada.
  • Zhang LH; Department of Medical Genetics, Center for Molecular Medicine and Therapeutics, BC Children's Hospital Research Institute, University of British Columbia, Vancouver, Canada.
  • Nazemi-Moghaddam N; Faculty of Pharmaceutical Sciences, University of British Columbia, Vancouver, Canada.
  • Elahi SM; Department of Production Platforms and Analytics, Human Health Therapeutics Research Center, National Research Council Canada, Montréal, Canada.
  • Ross CJD; Department of Production Platforms and Analytics, Human Health Therapeutics Research Center, National Research Council Canada, Montréal, Canada.
  • Stanimirovic DB; Department of Medical Genetics, Center for Molecular Medicine and Therapeutics, BC Children's Hospital Research Institute, University of British Columbia, Vancouver, Canada.
  • Hayden MR; Faculty of Pharmaceutical Sciences, University of British Columbia, Vancouver, Canada.
Hum Gene Ther ; 34(17-18): 927-946, 2023 09.
Article en En | MEDLINE | ID: mdl-37597209

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Hiperlipoproteinemia Tipo I Tipo de estudio: Risk_factors_studies Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2023 Tipo del documento: Article

Texto completo: 1 Base de datos: MEDLINE Asunto principal: Hiperlipoproteinemia Tipo I Tipo de estudio: Risk_factors_studies Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2023 Tipo del documento: Article